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已按「庞贝病」检索，对应国际通用词 Pompe disease
共找到 24 项正在招募的试验
数据更新于 00:19，每 5 分钟自动同步A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
United States
年龄 18 Years – 65 Years
AskBio Inc
Pompe Disease Registry Protocol
United States、Argentina、Australia、Belgium、Brazil 等 12 国
年龄 不限 – 不限
Genzyme, a Sanofi Company
Comparing Efficacy of 8-Week and 12-Week Faricimab Initial Follow-Up Treatment Intervals
Czechia
年龄 不限 – 不限
Faculty Hospital Kralovske Vinohrady
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
United States
年龄 18 Years – 75 Years
Denali Therapeutics Inc.
A Clinical Trial Evaluating the Safety and Efficacy of a New Light Combination Therapy Addressing Intermediate AMD
Italy
年龄 50 Years – 不限
Oculox Technologies SA
Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
United States
年龄 不限 – 不限
Duke University
Pompe Pregnancy Sub-Registry
United States、Australia、Belgium、Brazil、Croatia 等 9 国
年龄 不限 – 不限
Genzyme, a Sanofi Company
Cognitive and Neurological Pathologies in Pompe Disease
United States
年龄 0 Years – 18 Years
Duke University
Long-Term Development of Muscular Dystrophy Outcome Assessments
United States
年龄 6 Years – 50 Years
Virginia Commonwealth University
Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology
Belgium
年龄 18 Years – 不限
Centre Hospitalier Universitaire de Liege
A Long-term Study for the Outcome of Pompe Disease
Taiwan
年龄 不限 – 不限
National Taiwan University Hospital
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
United States、Germany、Italy、Netherlands、Taiwan 等 6 国
年龄 不限 – 17 Years
Amicus Therapeutics