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已按「阵发性睡眠性血红蛋白尿」检索,对应国际通用词 paroxysmal nocturnal hemoglobinuria

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正在招募III 期NCT07154745

A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently

Brazil、Canada、Italy、Poland、South Korea 等 7 国

年龄 18 Years – 不限

Regeneron Pharmaceuticals

正在招募III 期NCT06934967

Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients

United States、Brazil、Colombia、Germany、Italy 等 6 国

年龄 2 Years – 18 Years

Novartis Pharmaceuticals

正在招募I 期中国有中心NCT07462780

A Phase I Clinical Trial to Evaluate CMS-D017 Following Single and Multiple Doses in Healthy Participants

China

年龄 18 Years – 55 Years

Shenzhen Kangzhe Biotechnology Co., Ltd.

正在招募不适用NCT07877727

Enhancing the Clinical Management of CMF Through a National Pediatric and Adult Network Based on Biological and Genetic Data

Italy

年龄 28 Days – 65 Years

Istituto Giannina Gaslini

正在招募I 期中国有中心NCT07760467

To Evaluate Safety, Tolerability, PK/PD & Food Effect of Single/Multiple Oral TUL321 Capsules in Healthy Participants.

China

年龄 18 Years – 45 Years

Zhuhai United Laboratories Co., Ltd.

正在招募I 期 / II 期NCT07187401

A First-in-Human Safety and Efficacy Study of ALN-CFB, a Small Interfering RNA (siRNA) Targeting Complement Factor B, in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria With Persistent Anemia on a C5 Inhibitor

Canada、South Korea、United Kingdom

年龄 18 Years – 不限

Regeneron Pharmaceuticals

正在招募不适用NCT06312644

Study of Ultomiris® (Ravulizumab) Safety in Pregnancy

United States、Australia、France、Germany、Italy 等 7 国

年龄 不限 – 不限

Alexion Pharmaceuticals, Inc.

正在招募III 期NCT05744921

A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works

Brazil、Canada、Colombia、Hungary、India 等 12 国

年龄 18 Years – 不限

Regeneron Pharmaceuticals

正在招募II 期中国有中心NCT06978699

A Phase II Study Evaluating the Efficacy and Safety of XH-S003 Capsules in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

China

年龄 18 Years – 不限

S-INFINITY Pharmaceuticals Co., Ltd

正在招募I 期 / II 期NCT05876312

Safety, Tolerability, PK and PD of ADX-038 in Healthy Participants and Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients

Australia、United Kingdom

年龄 18 Years – 不限

ADARx Pharmaceuticals, Inc.

正在招募不适用中国有中心NCT06931691

A Multi-center, Ambispective Cohort Study to Evaluate the Impact of Iptacopan for Adult Patients With PNH in China

China

年龄 18 Years – 80 Years

Novartis Pharmaceuticals

正在招募不适用NCT06411626

Home Reported Outcomes in PNH

United States

年龄 18 Years – 99 Years

Novartis Pharmaceuticals