查找临床试验
已按「阵发性睡眠性血红蛋白尿」检索,对应国际通用词 paroxysmal nocturnal hemoglobinuria
共找到 30 项正在招募的试验
数据更新于 00:23,每 5 分钟自动同步A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently
Brazil、Canada、Italy、Poland、South Korea 等 7 国
年龄 18 Years – 不限
Regeneron Pharmaceuticals
Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients
United States、Brazil、Colombia、Germany、Italy 等 6 国
年龄 2 Years – 18 Years
Novartis Pharmaceuticals
A Phase I Clinical Trial to Evaluate CMS-D017 Following Single and Multiple Doses in Healthy Participants
China
年龄 18 Years – 55 Years
Shenzhen Kangzhe Biotechnology Co., Ltd.
Enhancing the Clinical Management of CMF Through a National Pediatric and Adult Network Based on Biological and Genetic Data
Italy
年龄 28 Days – 65 Years
Istituto Giannina Gaslini
To Evaluate Safety, Tolerability, PK/PD & Food Effect of Single/Multiple Oral TUL321 Capsules in Healthy Participants.
China
年龄 18 Years – 45 Years
Zhuhai United Laboratories Co., Ltd.
A First-in-Human Safety and Efficacy Study of ALN-CFB, a Small Interfering RNA (siRNA) Targeting Complement Factor B, in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria With Persistent Anemia on a C5 Inhibitor
Canada、South Korea、United Kingdom
年龄 18 Years – 不限
Regeneron Pharmaceuticals
Study of Ultomiris® (Ravulizumab) Safety in Pregnancy
United States、Australia、France、Germany、Italy 等 7 国
年龄 不限 – 不限
Alexion Pharmaceuticals, Inc.
A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works
Brazil、Canada、Colombia、Hungary、India 等 12 国
年龄 18 Years – 不限
Regeneron Pharmaceuticals
A Phase II Study Evaluating the Efficacy and Safety of XH-S003 Capsules in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
China
年龄 18 Years – 不限
S-INFINITY Pharmaceuticals Co., Ltd
Safety, Tolerability, PK and PD of ADX-038 in Healthy Participants and Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients
Australia、United Kingdom
年龄 18 Years – 不限
ADARx Pharmaceuticals, Inc.
A Multi-center, Ambispective Cohort Study to Evaluate the Impact of Iptacopan for Adult Patients With PNH in China
China
年龄 18 Years – 80 Years
Novartis Pharmaceuticals
Home Reported Outcomes in PNH
United States
年龄 18 Years – 99 Years
Novartis Pharmaceuticals