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已按「地中海贫血」检索,对应国际通用词 thalassemia

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共找到 12 项正在招募的试验(在欧美日韩等发达国家设有中心)

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正在招募I 期 / II 期NCT03653338

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

United States

年龄 5 Years40 Years

Paul Szabolcs

正在招募不适用NCT06073860

A Post-Marketing Surveillance Study to Assess Safety of Luspatercept in Korean Patients With Myelodysplastic Syndrome or β-thalassemia

South Korea

年龄 19 Years不限

Bristol-Myers Squibb

正在招募不适用NCT04872179

International Registry of Patients With Alpha Thalassemia

United States

年龄 不限不限

University of California, San Francisco

正在招募不适用NCT03775954

Fetal Electrophysiologic Abnormalities in High-Risk Pregnancies Associated With Fetal Demise

United States

年龄 18 Years不限

Medical College of Wisconsin

正在招募II 期NCT04099966

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

United States

年龄 1 Day30 Years

Mitchell Cairo

正在招募III 期NCT07517133

A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia

United States

年龄 1 Year17 Years

Agios Pharmaceuticals, Inc.

正在招募不适用NCT03937817

Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants

United States

年龄 18 Years70 Years

National Institute of Allergy and Infectious Diseases (NIAID)

正在招募不适用NCT05508932

Atrial Fibrillation in Beta-Thalassemia

Italy

年龄 18 Years不限

University Hospital of Ferrara

正在招募不适用NCT07672275

Transfusion-Related Changes in Oxidative Stress Biomarkers in Neonates

Austria

年龄 5 Minutes5 Months

Medical University of Graz

正在招募I 期 / II 期NCT06364774

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

United States

年龄 18 Years40 Years

Children's Hospital of Philadelphia

正在招募不适用NCT06250595

European Rare Blood Disorders Platform (ENROL)

Spain

年龄 不限100 Years

Hospital Universitari Vall d'Hebron Research Institute

正在招募II 期NCT05693909

A Trial Testing SP-420 in Subjects With Transfusion-dependent β-thalassemia or Low-risk Myelodysplastic Syndromes

Denmark

年龄 18 Years不限

Pharmacosmos A/S