查找临床试验
已按「庞贝病」检索，对应国际通用词 Pompe disease
共找到 12 项正在招募的试验（在欧美日韩等发达国家设有中心）
数据更新于 11:18，每 5 分钟自动同步Registry of Patients Diagnosed With Lysosomal Storage Diseases
United States
年龄 不限 – 64 Years
University of California, San Francisco
Pompe Pregnancy Sub-Registry
United States、Australia、Belgium、Brazil、Croatia 等 9 国
年龄 不限 – 不限
Genzyme, a Sanofi Company
A Clinical Trial Evaluating the Safety and Efficacy of a New Light Combination Therapy Addressing Intermediate AMD
Italy
年龄 50 Years – 不限
Oculox Technologies SA
Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology
Belgium
年龄 18 Years – 不限
Centre Hospitalier Universitaire de Liege
Phrenic Nerve and Diaphragm Electrophysiology in Pompe Disease
Italy
年龄 18 Years – 不限
IRCCS National Neurological Institute "C. Mondino" Foundation
Avalglucosidase Alfa Pregnancy Study
United States
年龄 不限 – 不限
Sanofi
Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
United States
年龄 18 Years – 不限
University of Missouri-Columbia
A Global Prospective Observational Registry of Patients With Pompe Disease
United States、Austria、Belgium、Denmark、Germany 等 12 国
年龄 不限 – 不限
Amicus Therapeutics
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
United States、Germany、Italy、Netherlands、Taiwan 等 6 国
年龄 不限 – 17 Years
Amicus Therapeutics
Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
United States
年龄 不限 – 不限
Duke University
Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases
France
年龄 不限 – 不限
Assistance Publique Hopitaux De Marseille
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
United States
年龄 18 Years – 50 Years
University of California, San Francisco