查找临床试验

已按「杜氏肌营养不良」检索,对应国际通用词 Duchenne muscular dystrophy

试验不在中国怎么办?

共找到 12 项正在招募的试验(在欧美日韩等发达国家设有中心)

数据更新于 11:18,每 5 分钟自动同步
正在招募II 期NCT07287189

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

United States、Australia、Belgium、Canada、Poland 等 8 国

年龄 7 Years9 Years

Satellos Bioscience, Inc.

正在招募不适用NCT06755138

Research on the Relationship Between Scoliosis, Pain, Quality of Life, and Trunk Muscle Compensation Patterns Among Patients with Duchenne Muscular Dystrophy.

South Korea

年龄 11 Years30 Years

Seoul National University Hospital

正在招募不适用NCT00390104

Molecular Analysis of Patients With Neuromuscular Disease

United States

年龄 1 Week100 Years

Boston Children's Hospital

正在招募不适用NCT05016908

Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy

United States

年龄 5 Years不限

Massachusetts General Hospital

正在招募I 期 / II 期NCT04906460

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

United States、Jordan、United Kingdom

年龄 4 Years18 Years

Wave Life Sciences USA, Inc.

正在招募I 期 / II 期NCT07038824

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45

Belgium、Italy、Netherlands、Spain、United Kingdom

年龄 4 Years20 Years

Entrada Therapeutics, Inc.

正在招募不适用NCT07332013

Urinary Titin Biomarker in DMD

United States

年龄 2 Years10 Years

Children's Hospital of Philadelphia

正在招募不适用NCT07378553

Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies

France

年龄 5 Years60 Years

Nantes University Hospital

正在招募不适用NCT06839469

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

United States

年龄 5 Years不限

Columbia University

正在招募I 期 / II 期NCT07037862

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44

Belgium、Italy、Spain、United Kingdom

年龄 4 Years20 Years

Entrada Therapeutics, Inc.

正在招募IV 期NCT05412394

Once Weekly Infant Corticosteroid Trial for DMD

United States

年龄 1 Month30 Months

Anne M. Connolly

正在招募不适用NCT07092540

The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy

United States

年龄 0 Days3 Years

University of Rochester