查找临床试验
已按「杜氏肌营养不良」检索,对应国际通用词 Duchenne muscular dystrophy
共找到 51 项正在招募的试验(在欧美日韩等发达国家设有中心)
数据更新于 00:19,每 5 分钟自动同步Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
United States、Belgium、Canada、France、Germany 等 11 国
年龄 7 Years – 不限
Italfarmaco
A Remote Study Using Technology to Assess Outcomes in DMD
United Kingdom
年龄 1 Year – 3 Years
University of Oxford
Biomarker Development for Muscular Dystrophies
United States
年龄 5 Years – 不限
Massachusetts General Hospital
Urinary Titin Biomarker in DMD
United States
年龄 2 Years – 10 Years
Children's Hospital of Philadelphia
Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy
United States
年龄 8 Years – 18 Years
Vanderbilt University Medical Center
Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
United States
年龄 6 Years – 不限
University of Florida
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
United States、Canada、Italy、United Kingdom
年龄 0 Years – 17 Years
Solid Biosciences Inc.
Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
United States
年龄 5 Years – 不限
Columbia University
A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
United States
年龄 6 Years – 不限
ITF Therapeutics LLC
Invasive Home Ventilation in Denmark
Denmark
年龄 不限 – 不限
Copenhagen University Hospital, Rigshospitalet
Natural History of Duchenne Muscular Dystrophy
Belgium、France、Spain、United Kingdom
年龄 4 Years – 9 Years
Genethon
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
United States、Puerto Rico
年龄 2 Years – 不限
Catalyst Pharmaceuticals, Inc.