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已按「杜氏肌营养不良」检索,对应国际通用词 Duchenne muscular dystrophy

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共找到 51 项正在招募的试验(在欧美日韩等发达国家设有中心)

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正在招募II 期 / III 期NCT03373968

Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

United States、Belgium、Canada、France、Germany 等 11 国

年龄 7 Years – 不限

Italfarmaco

正在招募不适用NCT07423026

A Remote Study Using Technology to Assess Outcomes in DMD

United Kingdom

年龄 1 Year – 3 Years

University of Oxford

正在招募不适用NCT05019625

Biomarker Development for Muscular Dystrophies

United States

年龄 5 Years – 不限

Massachusetts General Hospital

正在招募不适用NCT07332013

Urinary Titin Biomarker in DMD

United States

年龄 2 Years – 10 Years

Children's Hospital of Philadelphia

正在招募I 期NCT07172971

Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy

United States

年龄 8 Years – 18 Years

Vanderbilt University Medical Center

正在招募II 期NCT07766980

Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients

United States

年龄 6 Years – 不限

University of Florida

正在招募I 期 / II 期NCT06138639

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

United States、Canada、Italy、United Kingdom

年龄 0 Years – 17 Years

Solid Biosciences Inc.

正在招募不适用NCT06839469

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

United States

年龄 5 Years – 不限

Columbia University

正在招募不适用NCT07127978

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

United States

年龄 6 Years – 不限

ITF Therapeutics LLC

正在招募不适用NCT07467187

Invasive Home Ventilation in Denmark

Denmark

年龄 不限 – 不限

Copenhagen University Hospital, Rigshospitalet

正在招募不适用NCT03882827

Natural History of Duchenne Muscular Dystrophy

Belgium、France、Spain、United Kingdom

年龄 4 Years – 9 Years

Genethon

正在招募不适用NCT06564974

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

United States、Puerto Rico

年龄 2 Years – 不限

Catalyst Pharmaceuticals, Inc.