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已按「脊髓性肌萎缩症」检索,对应国际通用词 spinal muscular atrophy

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共找到 12 项正在招募的试验(在欧美日韩等发达国家设有中心)

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正在招募不适用NCT05663008

Impairments of Neuro-muscular Communication in Motor-Neuron Disease: A Bio-Marker for Early and Personalised Diagnosis

Ireland

年龄 18 Years不限

University of Dublin, Trinity College

正在招募不适用NCT06321965

Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy

France

年龄 0 Years16 Years

Hospices Civils de Lyon

正在招募不适用NCT07332702

Long Read Analysis in Spinal Muscular Atrophy - LOREASI

France

年龄 18 Years不限

University Hospital, Rouen

正在招募III 期中国有中心NCT07221669

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

United States、Australia、Brazil、China、Japan

年龄 0 Days42 Days

Biogen

正在招募II 期 / III 期NCT06862596

Clinical Trial of Mexiletine Hydrochloride for Spinal and Bulbar Muscular Atrophy

Japan

年龄 18 Years80 Years

Masahisa Katsuno

正在招募不适用NCT06396325

A Registry Based Randomized-Controlled Trial of an Upper Limb Exergaming Intervention for Children and Adolescents With Spinal Muscular Atrophy

Canada

年龄 8 Years18 Years

Maryam Oskoui, MD, MSc, FRCPC, FAAN

正在招募III 期NCT07444476

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

United States

年龄 15 Years60 Years

Biogen

正在招募不适用NCT06839469

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

United States

年龄 5 Years不限

Columbia University

正在招募不适用NCT07136844

Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology

Belgium

年龄 18 Years不限

Centre Hospitalier Universitaire de Liege

正在招募II 期NCT06169046

A Placebo-controlled Study of Clenbuterol in Spinal and Bulbar Muscular Atrophy

Italy

年龄 18 Years75 Years

Gianni Soraru

正在招募不适用NCT07231549

CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain

Spain

年龄 不限不限

Fundació Sant Joan de Déu

正在招募II 期NCT07047144

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

United States、Belgium、France、Italy、Netherlands 等 7 国

年龄 不限2 Years

Scholar Rock, Inc.