戈谢病临床试验招募信息（全球在招）

这里汇总了全球正在招募患者的 戈谢病（国际通用名 Gaucher disease）新药临床试验，包含试验分期、招募状态、开展国家和研究团队联系方式，全部以中文呈现。数据实时来自全球最大的临床试验注册库 ClinicalTrials.gov。

正在招募的戈谢病新药试验

• An Exploratory Clinical Trial of VGN-R08b in Patients With Type II Gaucher Disease

  早期 I 期招募中中国NCT06272149

• Registry of Patients Diagnosed With Lysosomal Storage Diseases

  不适用招募中美国NCT05619900

• A Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher Disease

  I 期 / II 期招募中中国NCT06818838

• Study of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory Osteosarcoma

  I 期招募中美国NCT03721068

• Natural History of Glycosphingolipid Storage Disorders and Glycoprotein Disorders

  不适用招募中美国NCT00029965

• GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple Myeloma

  不适用招募中西班牙NCT05992532

• A Study of the Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients With Gaucher Disease Type I

  不适用招募中中国NCT06162338

• Gaucher Disease Outcome Survey (GOS)

  不适用招募中美国NCT03291223

• PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  I 期招募中美国NCT04532047

• A Long-term Follow-up Study of Gaucher Disease

  不适用招募中美国NCT03190837

• International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  不适用招募中美国Argentina澳大利亚BelgiumNCT00358943

• Advancing Integrated Therapies for Gaucher Disease

  不适用招募中美国NCT07758816