阵发性睡眠性血红蛋白尿临床试验招募信息（全球在招）
这里汇总了全球正在招募患者的 阵发性睡眠性血红蛋白尿（国际通用名 paroxysmal nocturnal hemoglobinuria）新药临床试验，包含试验分期、招募状态、开展国家和研究团队联系方式，全部以中文呈现。数据实时来自全球最大的临床试验注册库 ClinicalTrials.gov。本页同时覆盖PNH等说法。
正在招募的阵发性睡眠性血红蛋白尿新药试验
Investigation of Pharmacokinetics,Safety,and Pharmacodynamics of HSK39297 in Subjects With Hepatic Impairment
I 期招募中中国NCT07152288Danicopan PMS in Korea
不适用招募中South KoreaNCT07457151A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently
III 期招募中Brazil加拿大意大利PolandNCT07154745Study of Safety and Efficacy of MY008211A in Patients With Residual Anemia Despite Anti-C5 Antibody Treatment
III 期招募中中国NCT06932471A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works
III 期招募中加拿大ColombiaHungaryIndiaNCT05744921The International PNH Interest Group PNH Registry
不适用招募中美国NCT06524726Safety, Tolerability, PK and PD of ADX-038 in Healthy Participants and Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients
I 期 / II 期招募中澳大利亚英国NCT05876312Global PNH Patient Registry
不适用招募中美国NCT05755867A First-in-Human Safety and Efficacy Study of ALN-CFB, a Small Interfering RNA (siRNA) Targeting Complement Factor B, in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria With Persistent Anemia on a C5 Inhibitor
I 期 / II 期招募中加拿大South Korea英国NCT07187401A Phase I Clinical Trial to Evaluate CMS-D017 Following Single and Multiple Doses in Healthy Participants
I 期招募中中国NCT07462780MT2023-20: Hematopoietic Cell Transplant With Reduced Intensity Conditioning and Post-transplant Cyclophosphamide for Severe Aplastic Anemia and Other Forms of Acquired Bone Marrow Failure.
II 期招募中美国NCT06412497Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients
III 期招募中美国BrazilColombia德国NCT06934967
阵发性睡眠性血红蛋白尿试验不在中国大陆，还能参加吗？
可以尝试四条现实路径：查找国内同类试验、申请同情用药与扩展准入、赴境外研究中心入组、直接写信给申办方申请在华开展。本站提供中英文对照的咨询信模板，患者和家属填写基本情况即可生成。